12:00 AM
 | 
Sep 22, 2016
 |  BC Innovations  |  Distillery Therapeutics

Therapeutics: Hemoglobin subunit γ 1 (HBG1); HBG2; CRISPR-associated protein 9 (Cas9)

Hematology

INDICATION: Sickle cell disease (SCD)

Patient sample and cell culture studies suggest enhancing fetal hemoglobin production in hematopoietic stem and progenitor cells (HSPCs) using CRISPR-based gene editing could help treat...

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