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<div class="articleContainer"><div class="articleWrapper"><div class="articleContent"><h1 class="text title">In vivo adenine base editing corrects SCN1A deficiency in Dravet syndrome</h1><div class="byline">BC Staff</div><div class="date"></div>
    
    
    
    
    
    
    
    
    
    
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Broad Institute of Mit and Harvard

The Children's Hospital of Philadelphia

The Jackson Laboratory

Neurology

Sodium voltage-gated channel alpha subunit 1 (Nav1.1) (SCN1A)

In vivo adenine base editing corrects SCN1A deficiency in Dravet syndrome

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