Distillery Therapeutics


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<h1 class="text title" doc-editable="text" data-component-id="doc-1ef7l992d0">Antisense oligos against transcription factor DUX4 for a muscular dystrophy</h1><div class="byline ng-tns-c17-4 ng-star-inserted" data-component-id="doc-1ef7l9he70">
    <span class="ng-tns-c17-4" doc-editable="text">By Claire Quang, Staff Writer</span>
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

University of Alberta

The George Washington University

DISEASE CATEGORY: MusculoskeletalINDICATION: Muscular dystrophy......

Musculoskeletal

Muscular dystrophy

Double homeobox 4 (DUX4)

Antisense oligos against transcription factor DUX4 for a muscular dystrophy

DISEASE CATEGORY: Musculoskeletal<br/>INDICATION: Muscular dystrophy Antisense oligonucleotide therapies targeting DUX4 could treat facioscapulohumeral muscular dystrophy (FSHD), which is caused by