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FDA panel concludes Translarna data inconclusive in DMD

FDA's Peripheral and Central Nervous System Drugs Advisory Committee voted overwhelmingly that efficacy data for Translarna ataluren to treat nonsense mutations in Duchenne muscular dystrophy (DMD) were inconclusive.

Ten of 11 panel members voted that although it is possible Translarna from PTC Therapeutics Inc. (NASDAQ:PTCT)

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