FDA reviewers question efficacy of BioMarin's DMD therapy

In briefing documents released ahead of a Nov. 24 advisory committee meeting, FDA reviewers expressed doubts that Kyndrisa drisapersen from BioMarin Pharmaceutical Inc. (NASDAQ:BMRN) is effective to treat Duchenne muscular dystrophy (DMD). The reviewers intimated that the agency will use the meeting of the Peripheral and Central Nervous System Drugs Advisory Committee to

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