ARTICLE | Politics & Policy

BIO, PPMD partner in patient-centered research

December 11, 2015 2:29 AM UTC

The Biotechnology Industry Organization and Parent Project Muscular Dystrophy launched an initiative to share best practices in designing disease-specific patient preference studies. The parties intend to issue guidance for stakeholders outlining considerations for risk-benefit assessments to treat rare diseases.

The organizations have assembled a review committee comprising members of industry, academia and the patient community that will consider development of studies, interactions with regulators, uses of patient-preference data, and collaborations among stakeholders. ...