Log In
Print this Print this


  Manage Alerts
Collapse Summary General Information
Company Dimension Therapeutics Inc.
DescriptionAdeno-associated viral (AAV) vector delivering phenylalanine hydroxylase (PAH)
Molecular Target Phenylalanine hydroxylase (PAH)
Mechanism of Action 
Therapeutic ModalityGene therapy: Viral vector: Adeno-associated virus (AAV)
Latest Stage of DevelopmentDiscovery
Standard IndicationPhenylketonuria
Indication DetailsTreat phenylketonuria
Regulatory Designation

 Product Details
 Archive Items are loading loading
Collapse Summary Deals Information
 Deals Details
Get a free BioCentury trial today