ARTICLE | Distillery Therapeutics
Endocrine / Metabolic
December 20, 2016 7:38 PM UTC
Fruit fly studies suggest the generic mTOR inhibitor rapamycin could help treat Gaucher’s disease, which is caused by GBA mutations. In a GBA-knockout Drosophila model of Gaucher’s disease, rapamycin increased locomotor function and survival compared with vehicle. Next steps could include testing rapamycin in additional models of Gaucher’s disease...
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