ARTICLE | Clinical News
6R-BH4 sapropterin dihydrochloride: Phase IIa data
October 20, 2008 7:00 AM UTC
In a 16-week, dose-escalation, open-label, U.S. Phase IIa study in 32 patients with SCD, 6R-BH4 showed a dose-dependant improvement in endothelial dysfunction with the mean PAT score for all patients ...