BioCentury
ARTICLE | Distillery Therapeutics

Musculoskeletal

August 29, 2018 5:52 PM UTC

Cell culture and mouse studies suggest inhibiting miR-23b and miR-218 could help treat DM1. In myoblast cells from a DM1 patient, miR-23b and miR-218 antagomirs decreased disease-associated splicing d...