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ARTICLE | Distillery Therapeutics

Therapeutics: Chromosome 9 open reading frame 72 (C9orf72)

October 1, 2015 7:00 AM UTC

In vitro, yeast and fruit fly studies suggest restoring nucleocytoplasmic transport could help treat ALS caused by hexanucleotide repeat expansions in C9orf72. Genetic screening in yeast and Drosophil...