ARTICLE | Distillery Therapeutics
Therapeutics: Chromosome 9 open reading frame 72 (C9orf72)
October 1, 2015 7:00 AM UTC
In vitro, yeast and fruit fly studies suggest restoring nucleocytoplasmic transport could help treat ALS caused by hexanucleotide repeat expansions in C9orf72. Genetic screening in yeast and Drosophil...