BioCentury
ARTICLE | Distillery Therapeutics

Therapeutics: Galactosylceramidase (GALC)

April 30, 2015 7:00 AM UTC

Mouse studies suggest combining GALC gene therapy, the sphingolipid synthesis inhibitor L-cycloserine and bone marrow transplantation could help treat globoid cell leukodystrophy (Krabbe disease). Kra...