BioMarin amends Phase III of hemophilia A gene therapy

BioMarin Pharmaceutical Inc. (NASDAQ:BMRN) increased enrollment in a Phase III trial of valoctocogene roxaparvovec (formerly BMN 270) to treat severe hemophilia A and reported long-term data from a Phase I/II trial of the gene therapy in the indication.

BioMarin increased enrollment to 130 patients

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