ARTICLE | Distillery Therapeutics
Cardiovascular
January 23, 2019 12:07 AM UTC
Patient sample studies suggest CRISPR-mediated editing of the B isoform of LAMP2 could help treat Danon disease, a cardiomyopathy caused by a loss-of-function LAMP2 point mutations. In cardiomyocytes ...
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Lysosomal-associated membrane protein-2 (LAMP2) (LAMPB) (CD107b)