BioCentury
ARTICLE | Distillery Therapeutics

Neurology

December 19, 2017 8:54 PM UTC

Mouse and rat studies suggest inhibiting PMP22 could help treat Charcot-Marie-Tooth 1A (CMT1A) disease. In a mouse model of CMT1A, subcutaneous injection of an antisense oligonucleotide (ASO) targetin...