BioCentury
ARTICLE | Distillery Therapeutics

Neurology

January 3, 2017 11:03 PM UTC

In vitro and mouse studies suggest locked nucleic acid (LNA) antisense oligonucleotides targeting CTG repeats in mutant HTT (LNA-CTG) could help treat HD. In human fibroblasts from HD patients, LNA-CT...

BCIQ Target Profiles

Huntingtin (HTT)