ARTICLE | Clinical News
Retrophin preclinical data
September 2, 2013 7:00 AM UTC
In mice with a PKAN-like phenotype, RE-024 led to a 92.5% survival rate vs. 0% for placebo at 2 weeks (p<0.0001). RE-024 is a phosphopantothenate molecule that restores disruption in coenzyme A biosyn...