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Kalydeco, ivacaftor (VX-770)

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Company Vertex Pharmaceuticals Inc.
DescriptionSmall molecule potentiator of cystic fibrosis transmembrane conductance regulator (CFTR)
Molecular Target Cystic fibrosis transmembrane conductance regulator (CFTR)
Mechanism of ActionCFTR stabilizer
Latest Stage of DevelopmentMarketed
IndicationCystic fibrosis (CF)
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