Log In
Print this Print this

AT982 (formerly AT002)

  Manage Alerts
Collapse Summary General Information
Company Audentes Therapeutics Inc.
DescriptionAdeno-associated viral serotype 9 (AAV9) vector carrying the acid alpha glucosidase (GAA) gene
Molecular Target
Mechanism of ActionGene therapy
Therapeutic ModalityGene therapy: Viral vector: Adeno-associated virus (AAV)
Latest Stage of DevelopmentPreclinical
Standard IndicationPompe's disease
Indication DetailsTreat Pompe's disease
Regulatory Designation

 Product Details
 Archive Items are loading loading
Collapse Summary Deals Information
 Deals Details
Get a free BioCentury trial today